READING GENE THERAPY

first-in-class drug/medication

a drug that utilizes a new and unique mechanism of action to treat a specific medical condition

critical limb ischemia

thiếu máu nghiêm trọng ở chi

lippo protein lipase deficiency

the body cannot break down fat from digested food

cystic fibrosis

xơ nang

sickle cell anaemia

bệnh hồng cầu hình liềm

adrenoleukodystrophy

a genetic disorder connected to the X chromosome. It affects the nervous system and adrenal glands. Symptoms of ALD often include behavioral and cognitive changes. ALD affects males more than females.

haemophilia

a rare, genetic blood disorder that happens when your blood doesn't clot enough to make your bleeding slow down or stop ( máu khó đông)

clinical research

a field of study that involves the use of human subjects or data/samples from humans to improve understanding of health and disease (nghiên cứu lâm sàng)

therapeutic

relating to therapy

ornithine transcarbamylase

an enzyme involved in the urea cycle, a metabolic pathway that helps remove excess nitrogen from the body

X-linked severe combined immunodeficiency (X-SCID)

an inherited disorder of the immune system that occurs almost exclusively in males (suy giảm miễn dịch kết hợp nặng)

leukemia

a type of cancer that affects blood cells and bone marrow, characterized by the uncontrolled growth of abnormal white blood cells.

intuition

trực giác

jurisdiction

quyền xét xử

The court has no jurisdiction in/over cases of this kind.

School admissions are not under/within our jurisdiction.