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Disorders of Carbohydrate Metabolism
glycogen storage disease
G6PD deficiency
Disorders of Amino Acid Metabolism
phenylketonuria
tyrosinemia
maple syrup urine disease
glutamic acidemia type 1
Urea Cycle Disorder (or Urea Cycle Defects)
carbamoyl phosphate synthetase I deficiency
citrullinemia type II (citrin deficiency)
Disorders of Organic Acid Metabolism (Organic Acidurias)
alkaptonuria
combine masonic and methylmalonic acuduria (CMAMMA)
2-hydroxyglutaric ccidurias
Disorders of Steroid Metabolism
lipoid congenital adrenal hyperplasia
congenital adrenal hyperplasia
Disorders of Fatty Acid Oxidation and Mitochondrial Metabolism
medium-chain acyl-coenzyme A dehydrogenase deficiency (MCADD)
Disorders of Porphyrin Metabolism
acute intermittent porphyria
Disorders of Purine or Pyrimidine Metabolism
Lesch-Nyhan syndrome
AMPD1 deficiency (MADD)
Disorders of Mitochondrial Function
Kearns-Sayre syndrome
Disorders of Peroxisomal Function
Zellweger syndrome
Lysosomal Storage Disorders
Gaucher’s disease
Niemann-Pick disease