Paragraph 2 - Gene Therapy Design and Mechanism of Action

0.0(0)
Studied by 0 people
call kaiCall Kai
learnLearn
examPractice Test
spaced repetitionSpaced Repetition
heart puzzleMatch
flashcardsFlashcards
GameKnowt Play
Card Sorting

1/13

encourage image

There's no tags or description

Looks like no tags are added yet.

Last updated 8:35 PM on 5/2/26
Name
Mastery
Learn
Test
Matching
Spaced
Call with Kai

No analytics yet

Send a link to your students to track their progress

14 Terms

1
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout

what casgevy doesn’t do
    what its designed to do
    what it can replace
    whatapproach does it use
    what kind of cells do they use
    what happens to the cells

2
New cards

Paragraph 2

Gene Therapy Design and Mechanism of Action

3
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout 1

what casgevy doesn’t do

4
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout 2

what its designed to do

5
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout 3

what it can replace

6
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout 4

whatapproach does it use

7
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout 5

what kind of cells do they use

8
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action layout 6

what happens to the cells

9
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action what casgevy doesn’t do

directly repair the mutant HBB gene

10
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action what its designed to do

circumvent the defect by reactivating fetal haemoglobin (HbF),

11
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action what it can replace

the function of the mutant adult haemoglobin.

12
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action whatapproach does it use

ex vivo

13
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action what kind of cells do they use

patients CD34+ haematopoietic stem cells

14
New cards

Paragraph 2 - Gene Therapy Design and Mechanism of Action what happens to the cells

collected and edited in a laborator