Theranostics in Cancer

THERANOSTICS IN CANCER TREATMENT

Course Information

  • Course Title: Theranostics in Cancer Treatment

  • Theme: Theranostics - Now and the Future

  • Lecturer: ally-Ann Cryan

  • Date: 05 Nov 2025

  • Institution: RCSI Royal College of Surgeons in Ireland

LEARNING OUTCOMES

  • Outline what is meant by theranostics in the context of cancer therapy:

    • Understand the fusion of diagnostic methods with therapeutic agents for enhanced cancer treatment.

  • Discuss the importance of precision medicine for enhanced treatment outcomes:

    • Emphasize tailor-made treatments based on individual genetic and molecular profiles.

  • Provide examples of molecularly targeted treatments for cancer:

    • Review specific therapeutic modalities focusing on molecular targets unique to certain cancers.

WHAT IS THERANOSTICS

  • Definition:

    • “Theranostics” is the combination of diagnosing and therapeutic processes to treat diseases, particularly cancers.

    • The term is a blend of Therapeutic and Diagnostic.

  • Significance:

    • Theranostics aids in identifying the most effective treatment protocols by combining diagnosis with personalized therapy.

THERANOSTICS: THE POSSIBLE SCENARIOS

  1. Therapeutic followed by Diagnostic:

    • Example: A drug that demonstrates efficacy in treatment, but only for specific patient subsets; thus, new diagnostic methods identify suitable patients.

  2. Diagnostic followed by Therapeutic:

    • A diagnostic test that can distinguish patient types or disease stages, allowing more accurate therapy selection.

  3. Co-development:

    • Example: Herceptin and HerceptTest for breast cancer, where the therapy and diagnostic tools were developed and approved simultaneously.

THERAPEUTIC FOLLOWING BY DIAGNOSTIC

  • Example of Biomarkers:

    • Oncotype DX 21 genomic test:

    • One of the first validated molecular tests for providing a risk stratification model predicting benefits of adjuvant chemotherapy for breast cancer patients.

DIAGNOSTIC FOLLOWED BY THERAPEUTIC

  • Use of Tumor-Specific Ligand:

    • A ligand that can be employed for both imaging and therapeutic applications, depending on the chosen radioisotope.

  • Example: Use of [68Gallium/177Lutetium] PSMA (prostate-specific membrane antigen):

    • PET imaging is performed before and after treatment in prostate cancer patients.

    • Therapeutic radiopharmaceuticals labeled with β-emitting radionuclides are utilized to damage tumor cells through energy loss over tissue traversal.

  • Positron Emission Tomography (PET):

    • A nuclear imaging technique enabling radionuclide visualization and quantified assessment in non-toxic amounts.

CO-DEVELOPMENT: COMPANION DIAGNOSTICS

  • Herceptin® (Trastuzumab):

    • A monoclonal antibody used for HER2-positive breast cancer treatment.

  • FDA Approval:

    • First approval received in 1998, with the HER2 diagnostic test (HercepTest) simultaneously authorized for assessing HER2 protein levels.

  • Clinical Relevance:

    • Approximately 20-25% of breast cancer patients overexpress HER2, which correlates with a more aggressive disease form.

    • These cancers may show less responsiveness to standard treatment approaches including selected chemotherapy regimens and hormone therapies.

    • The diagnostic test detects elevated HER2 levels in tumors and excess copies of the HER2 gene, indicating potential efficacy of Herceptin.

EARLY THERANOSTIC DEVELOPMENT

  • Historical Efforts (1930s):

    • Initial studies on phosphorous-32, a radioactive isotope for bone tumor treatment, were not commercially developed.

  • Advancements in Radiochemistry:

    • Synthetic approaches led to the creation of iodine-131, generated in cyclotrons at MIT.

    • Early assessments in rabbits, progressing to human trials for thyroid cancer and hyperthyroid conditions.

    • Function of Iodine-131:

    • Iodine uptake by the thyroid gland results in imaging and selective tissue destruction, achieving a 90% cure rate for patients.

THERANOSTICS IN THE CLINIC

  • Current Approvals:

    • Theranostics are approved for use in conditions such as thyroid disease, neuroendocrine tumors, and prostate cancer using nuclear medicine protocols.

  • Theranostic Approach:

    • Basis involves a ligand specifically binding to target cells and being chemically linked with a radioisotope for diagnostic or therapeutic applications.

    • Employing the same ligand with different radionuclides enhances targeting precision and minimizes side effects.

NUCLEAR MEDICINE

  • Radionuclide Therapy Definition:

    • Application of an unstable nuclide with a targeting vector to selectively deliver therapeutic radiation to malignant cells.

  • Theranostic Framework:

    • Involves using a duo of radiopharmaceuticals for imaging and treatment, which demands careful selection of radionuclides, as most radiopharmaceuticals lack the proper emission characteristics for both purposes.

NUCLEAR THERANOSTIC AGENTS

  • Comprehensive review citations:

    • Shrivastava, S., et al (2019) explores targeted diagnosis and therapy approaches.

THERANOSTICS IN THE CLINIC: COMPONENTS

  • Theranostics consist of:

    • A ligand to target diseased cells.

    • A radionuclide for therapy or imaging.

    • A linker to attach the ligand to the radionuclide.

  • Examples of Agents:

    Radionuclide

    Linker

    Ligand

    Indication

    Status

    Iodine-131

    None

    None

    Imaging and treatment of thyroid cancer

    Approved

    Iodine-123

    None

    Octreotide

    Imaging of neuroendocrine tumors

    Approved

    Lutetium-177

    DOTA

    Octreotide

    Treatment of neuroendocrine tumors

    Approved (Sandoz, Erasmus Medical Center)

    Gallium-68

    Lutetium-177

    DOTA

    Diagnosis of metastatic castration-resistant prostate cancer

    Phase 3 clinical trial

THERANOSTICS – NEUROENDOCRINE TUMORS

  • Lutathera®:

    • Utilized in treating unresectable or metastatic progressive somatostatin receptor-positive neuroendocrine tumors (GEP-NETs) in adults.

    • FDA approval in 2018, EMA approval in 2017.

    • Mechanism: Combines a radionuclide with a peptide binding to specific receptors on tumor cells while sparing normal tissue.

    • Diagnostic Radionuclide: [68Ga]-DOTA-TATE; Therapeutic Radionuclide: [177Lu]Lu-DOTA-TATE.

THERANOSTICS – PROSTATE CANCER

  • [177Lu]Lu-PSMA-617 (Pluvicto®):

    • FDA approved in 2022.

    • Targets prostate-specific membrane antigen, overexpressed in prostate tumor tissues but minimally expressed in normal tissues.

    • Established PSMA targeting agents for imaging and therapeutic applications.

  • Purpose of PSMA-617:

    • Identified as a treatment option for patients with advanced prostate cancer resistant to hormone deprivation therapy.

THERANOSTIC NANOPARTICLES: EXAMPLES IN CANCER

  • Factors Influencing Cancer Targeting:

    • Biodistribution of Drug: Role of the reticuloendothelial system (RES) and its clearance mechanisms.

    • Tumor Microenvironment Characteristics:

    • Overexpression of receptors and enzymes.

    • Presence of a hypoxic core and acidic environment due to metabolic activities.

    • Formation of aberrant vascular networks.

    • Existence of leaky vessels with inadequate lymphatic drainage.

    • Enhanced Penetration & Retention (EPR Effect): Heightened targeting ability resulting from unique tumor characteristics.

EXAMPLES OF NANOTHERANOSTICS IN CANCER

  1. Gold Nanoparticles:

    • Therapeutic Agent: Doxorubicin conjugated to gold nanoparticles (AuNP), used for in vivo imaging with fluorescence.

    • Targeting Moiety: Peptide substrate CPLGLAGG informed by Chen et al. (2013).

  2. Neural Cell Adhesion Molecule (NCAM)-targeted liposomes:

    • Nanocarrier: Liposomes laden with doxorubicin.

    • Diagnostic Agent: Gadolinium derivative for MRI visualization, referenced by Grange et al. (2010).

  3. Dendrimer Entrapped Gold Nanoparticles:

    • Nanocarrier: Dendrimer formulation facilitating imaging (CT) and apoptosis in cancer cells by targeting αvβ3 integrin.

CONCLUSION

  • The exploration of theranostic strategies showcases the transition towards more personalized cancer management approaches leveraging diagnostic and therapeutic synergies.

ADITIONAL CLASS INFORMATION

  • Next Session: Introduction to Nanoparticle Characterisation on November 18th, 2025.

  • Location: Dispensing Lab (Bring laptop for interactive component).