MedChem Discussion Nov 6, 2023
Introduction to Drug Metabolism
Focus on Phase II Metabolism
Xenobiotic Metabolism
Three main processes: Absorption, Metabolism, Excretion
Phases of Metabolism:
Phase I (Functionalization)
Involves oxidation, reduction, or hydrolysis.
Enzymes include:
Cytochrome P450 (CYP)
Flavin-containing monooxygenase
Dehydrogenase
Esterases
Results in more polar metabolites.
Phase II (Conjugation reactions)
Involves conjugation, which improves water solubility and excretion.
Enzymes include:
Glutathione transferase (GST)
UDP-glucuronyl transferase (UGT)
Sulfotransferase (SULT)
Acetyltransferase
Methyltransferase
Human CYP450 Enzymes
Major isoforms and their abundance:
CYP3A4: 23% contribution to drug metabolism (50% hepatic abundance)
Other notable isoforms:
CYP2E1 (12%)
CYP2D6 (2%)
CYP2C9 (20%)
CYP2C8 (14%)
CYP2C19 (4%)
CYP2A6 (15%)
CYP1A2 (10%)
Role in drug metabolism varies by family and specific isoenzyme.
Properties of Phase II Metabolism
Conjugation of small polar endogenous molecules (e.g., glucuronic acid, sulfate, amino acids) to metabolites.
Enhances water-solubility to facilitate renal excretion.
Detoxification: Traps electrophilic substances using glutathione, protecting DNA, RNA, and proteins.
Enzymes Involved in Phase I and II Metabolism
Prominent Phase I enzymes:
CYP1A1/2, CYP2D6, CYP3A4 and others
Phase II enzymes:
UGT, SULT, NAT, GST
Each enzyme plays a crucial role in the metabolism of specific drugs.
Metabolic Reactions in Phase II
Conjugation Reactions
Glycination: Transfer of amino acids.
Glucuronidation: Addition of glucuronic acid operates via UDP-glucuronyl transferase.
Sulfation: Involves sulfate transfer via sulfotransferases, utilizing PAPS.
Acetylation: Uses Acetyl-CoA with N-acetyltransferases.
Methylation: Involves SAM (S-adenosyl methionine) for transferring methyl groups via methyltransferases.
Examples of Substrates for Conjugation
Glucuronidation: Effective on substrates such as acetaminophen, morphine.
Sulfation: Target substrates include a-methyldopa, albuterol.
Acetylation: Significant for drugs like procainamide, leading to detoxification.
Structural Alerts in Drug Metabolism
Common structural alerts could indicate susceptibility to metabolic activation.
Includes functional groups like anilines, phenols, and aromatics.
Identifies compounds potentially leading to toxic metabolites.
Key Takeaways
Drug metabolism comprises two major phases, evolving from functionalization (Phase I) to conjugation (Phase II).
Understanding specific enzymes and their substrates is crucial for predicting metabolic pathways and potential drug interactions.