Cystic fibrosis is a genetic disorder affecting 1 in 3600 children in Canada.
It can be detected prenatally for at-risk couples and through newborn screening with blood and urine tests.
Genetic Aspect
CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) acts as a channel for chloride ions.
Disruption of chloride ion transport results in altered water flow, leading to increased viscosity of secretions throughout the body.
Carrier Frequency
Approximately 1 in 25 individuals in Canada are carriers of the CF gene.
The carrier rate increases to 1 in 20 for Quebecois.
Pathophysiology of Cystic Fibrosis
Sweat glands excrete excessive chloride leading to:
Electrolyte imbalances.
Dehydration symptoms.
Salty forehead on kissing a baby is an indication of cystic fibrosis.
Effects on Pancreas and Mucus Secretion
Blockage of pancreatic canals prevents secretion of enzymes necessary for fat and protein digestion.
Nutrient malabsorption results in poor growth and floating stools due to fats in stool.
Accumulation of thick mucus in tracheobronchial glands results in:
Frequent coughing.
Trapped air in smaller airways causing atelectasis.
Increased risk of bacterial infections and respiratory failure.
Common Associated Conditions
Nasal polyps and recurrent sinusitis.
Male infertility due to thick seminal fluid; female infertility due to thick cervical mucus.
Diagnosis
CF can be diagnosed in early childhood (within first 6 months) or in adulthood when symptoms are subtle.
Signs and symptoms include:
Salty sweat.
Repeated respiratory infections.
Failure to thrive.
Floating stools.
Examination includes:
General appearance.
Work of breathing (WOB).
Cough and sputum analysis.
Clubbing of fingers and toes.
Height assessment.
Diagnostic Tests
Sweat chloride test.
Chest X-ray.
Pulmonary function test.
Blood tests (including vitamin and pancreatic enzyme levels).
Fecal analysis for enzymes and fats.
Management Goals
Maximize lung function.
Liquefy secretions to decrease complications and bacterial infections.
Daily chest physiotherapy to mobilize secretions.
Techniques for secretion clearance include:
Postural drainage.
Percussion.
Vibration.
Positive expiratory pressure (PEP) masks.
Autogenic drainage (for older children).
Therapeutic Management
Physical Exercise to promote overall health.
Medications:
Bronchodilators (e.g., Ventolin).
Corticosteroids (e.g., Flovent).
Antibiotics.
Mucolytics (e.g., Pulmozyme), which reduce mucus viscosity by degrading DNA and its components.
Side effects of Pulmozyme can include voice changes and rashes.
Nasal Corticosteroids and Acetylcysteine (also known as a respiratory mucolytic):
It attracts water towards mucus, thinning it.
Hypertonic saline also increases salt in airways to attract water and thin mucus.
Potential side effects include increased cough and sore throat.
Nutritional Considerations
Recommended supplements include vitamins A, D, E, K, iron, zinc, and laxatives.
Encourage intake of salty foods to help manage electrolyte balance.
Conclusion
Cystic fibrosis is not curable but is treatable with proper management strategies, aimed at increasing growth, improving quality of life, and minimizing complications.