Friday, December 6th Lecture Notes

  • In eukaryotes, the cell must process its primary transcripts to produce functional, translatable mRNAs

    • For many eukaryotic genes, protein expression is regulated at the level of RNA processing, particularly by alternative splicing

  • Some genes products are processed in a single, reproducible pattern:

    • All introns are removed

    • The exons flanking each intron are spliced together with a phosphodiester bond

  • Overview of the Splicing Reaction

    • Splicing occurs in two steps:

      • The 5’ splice site is cut, with the 5’ end of the intron forming a covalent bond to a branch site in the intron

      • The 3’ splice site is then cut, and the lariat-shaped intron is removed

        • A new phosphodiester bond is formed joining the ends of the two exons

    • Both reactions are catalyzed by a molecular machined called the spliceosome

  • However, many eukaryotic gene products undergo alternative splicing (two or more different patterns of exon usage)

    • In humans, it is estimated that 94% of all protein-coding genes exhibit some degree of alternative splicing

  • Alternative splicing permits a single pre-mRNA to produce different isoforms of the same protein

    • The protein troponin plays a role in muscle contraction

      • The gene has five potential exons, and its pre-mRNA can undergo two different patterns of splicing:

        • Exons 1-2-3-5 can be spliced to produce the a isoform

        • Exons 1-2-4-5 can be spliced to produce the B isoform

  • Important Message:

    • Alternative splicing of troponin allows a single gene to synthesize two protein isoforms that are similar but structurally and functionally distinct

    • Individual muscle cells can vary the ratio of a and B troponin they produce, fine-tuning the properties of the cell

  • When alternative splicing occurs, the spliceosome chooses to cut at some potential splice sites, while skipping over other potential splice sites

    • In a troponin, the downstream end of exon 2 (5’ splice site) is cut and joined to the upstream end of Exon 3 (3’ splice site)

    • In B troponin, the downstream end of Exon 2 (5’ splice site) is cut and joined to the upstream end of Exon 4 (3’ splice site)

  • Several factors influence which splice sites are actually used during alternative splicing:

    • Some splice sites preferentially pair with one another due to specific features of their RNA sequences

    • A given cell can turn splice sites “on-or-off” by expressing proteins that will bind to the pre-mRNA near that splice site

      • Splice repressor proteins direct the spliceosome away from a potential splice site

      • Splice activator proteins direct the spliceosome to use a potential splice site

  • Variations in Splice Site Sequence

    • Both 5’ and 3’ splice sites are marked by somewhat variable base sequences

    • In general, the spliceosome can use a splice site if its sequence is > 60% consensus

    • The spliceosome can preferentially pair a particular 5’ splice site to one particular 3’ splice site solely because they match in terms of their base sequences

  • Another important factor in alternative splicing can be the presence of 2 or more core promoters

    • If a gene is transcribed from multiple promoters, it will produce multiple isoforms with different 5’ exons

  • Like humans, the fruit fly Drosophila uses an XY system of chromosomal sex determination

    • Females are XX; males are XY

    • The X and Y chromosomes of flies are not homologous to the X and Y chromosomes of humans (they contain completely different sets of genes)

    • In addition, the mechanism of sex determination in flies is different from humans or other mammals

  • In humans, the presence or absence of a Y chromosome determines whether the embryo develops male or female characteristics

  • In Drosophila, it is the ratio of X chromosomes to autosomes (non-sex chromosomes) that determines gender

    • A female fruit fly has 2 X chromosomes and 2 copies of each autosome

      • 1.0 ratio

    • A male fruit fly has 1 X chromosome and 2 copies of each autosome

      • 0.5 ratio

    • Unlike humans, an XXY fly develops a female anatomy

  • Alternative splicing plays a central role in the sex determination of Drosophila

    • There are four key genes:

      • Doublesex (dsx)

      • Sex-lethal (Sxl)

      • Transformer (tra)

      • Transformer-2 (tra-2)

    • All of these genes are autosomes (equal in number between males and females)

  • The doublesex gene (dsx) encodes a zinc finger transcription factor

    • This transcription factor has distinct isoforms in males and females; it is the isoform of Doublesex protein expressed by the fly that causes the formation of male or female organs

  • The male and female isoforms of Dsx protein result from alternative splicing

    • The male isoform is Exon 3/5; the female isoform is exons ¾

    • Exon 4 gets spliced to an alternative 3’ UTR with a different polyA signal sequence

  • The gender-specific splicing of the dsx gene product is determined by three splice regulatory proteins:

    • Sex-lethal (Sxl) encodes a splice repressor protein

    • Transformer (tra) and transformer-2 (tra-2) encode splice activator proteins

  • Female Development

    • In a female embryo, Sxl protein binds to both its own Sxl pre-mRNA and the tra and tra-2 pre-mRNAs

    • In each case, this splice repressor protein prevents the inclusion of a male-specific exon in the final mRNA

    • The TraF and Tra2F proteins bind to the dsx pre-mRNA

      • These splice activator proteins attract the spliceosome to Exon 4, causing it to be included in the female isoform of Dsx protein

  • Male Development

    • In males, there is no expression of the Sxl protein

    • Rather, the spliceosome includes a male-specific exon in the Sxl mRNA

    • This male-specific exon contains an in-frame stop codon

    • Hence, even though the male mRNA is longer than the female mRNA, it produces a short non-functional isoform of the Sxl protein

    • The failure to produce functional Sxl protein also results in the inclusion of male-specific exons in the tra and tra-2 mRNAs

      • These exons also contain premature stop codons, and result in the production of short, functionless proteins

    • In the absence of functional Tra and Tra-2 proteins, Exon 1 of the dsx mRNA is spliced to Exon 3, producing the male isoform

  • How does the female embryo come to have Sxl protein while the male embryo does not?

    • It depends upon gender-specific transcription

  • The Sxl gene has two different core promoters

    • The Pe or early promoter is only used during the earliest stages of embryonic development

    • As the embryo matures, transcription switches to the Pm or maintenance promoter

      • It has a different +1 site and produces a different Exon 1

  • Transcription from the Pe promoter depends on the relative concentrations of activator TFs Sisterless-a (Sis-a) and Sisterless-b (Sis-b) and the repressor TF Deadpan (dpn)

    • The dpn gene is on an autosome, so the amount of Dpn protein is constant in the two sexes

    • But the sis-a and sis-b genes are on the X chromosome, so females have 2 copies of each and males only have 1 copy of each

    • Hence, females make twice as much activator, and are able to transcribe from the Pe promoter

      • Males cannot

  • The use of two different Sxl promoters introduces another form of alternative splicing for the Sxl pre-mRNA:

    • Transcripts from the early Pe promoter do not require the Sxl protein to skip over the male-specific exon

    • Transcripts from the maintenance Pm promoter contain a different Exon 1, which does require functional Sxl protein (splice repressor) to skip over the male-specific exon

  • When Sxl is transcribed from the Pe promoter in female embryos, the spliceosome skips over the male-specific exon without any need for Sxl protein

    • When Sxl transcription switches to Pm promoter, the pre-mRNA has a different Exon 1; but with Sxl protein present, the male exon is still excluded from the mRNA

    • Male embryos do not use the Pe promoter

      • When they begin to use Pm, they have no Sxl protein and the male-specific exon is included in the mature mRNA

  • Mini Study Guide

    • mRNAs can be selectively spliced so that each gene may have multiple isoforms

    • Splicing is carried out by the Spliceosome, which recognizes sequences at splice junctions and removes the intron as a lariat structure

    • Splicing is regulated by splice activators and splice repressors

    • Genes can also have alternative start sites with alternative first exons

    • Understand how sex determination occurs in Drosophila