Cardiac Amyloidosis Imaging, Part 1: Amyloidosis Etiology and Image Acquisition

Amyloidosis Etiology and Characteristics

  • Amyloidosis is a group of diseases involving protein-based infiltrates in body tissues.

  • Cardiac amyloidosis was once considered rare, but noninvasive diagnostic testing has increased diagnoses.

What is Amyloidosis?

  • Amyloidosis is a group of diseases where protein-based infiltrates deposit in extracellular tissue space.

  • Proteins have many functions, such as catalyzing reactions, providing support, regulating transport, protecting against diseases, and coordinating cell signaling.

  • The human body has approximately 100,000 different proteins.

  • Proteins fold into precise shapes based on amino acid sequences, determining their function.

  • Proteins must maintain their shape to function correctly.

  • Misfolded proteins are typically disassembled and removed by proteasomes.

  • If misfolded proteins aren't removed, they accumulate in organs within extracellular tissue.

  • In amyloid disease, misfolded proteins form long, unbranched strings called fibrils resist dismantling.

  • Accumulation of amyloid fibrils impairs organ function.

  • Amyloid fibrils can deposit in any tissue or organ, leading to different clinical manifestations based on the affected organ and deposited protein.

  • Over 30 different amyloid diseases have been identified.

  • All amyloid is morphologically similar, despite the heterogeneity of organ involvement and clinical syndromes

Types of Amyloidosis

  • Classification is based on the abnormal protein involved and whether it is localized or systemic.

  • Localized amyloidosis affects a single organ, such as the skin, bladder, eyes, lungs, or brain. Alzheimer's disease is a localized form.

  • Systemic amyloidosis includes:

    • Monoclonal immunoglobulin light-chain amyloidosis (AL)

    • Transthyretin amyloidosis (ATTR)

    • Serum amyloid A amyloidosis

  • AL is caused by an overabundance and misfolding of light-chain proteins (antibody components produced by plasma cells).

    • There are two types of light chains: k and \lambda.

      • Light-chain fibrils can accumulate in the heart, kidneys, peripheral nerves, liver, skin, and gastrointestinal system.

      • AL is acquired, typically diagnosed in individuals over 50 years old, and has rapid progression.

  • ATTR results from the misfolding of transthyretin protein, which transports thyroxine and retinol-binding protein.

    • ATTR can affect multiple organs, including the heart, peripheral nerves, and autonomic nervous system.

    • When deposited in the autonomic nervous system, it can affect bladder, digestive, and genital function.

  • Serum amyloid A amyloidosis is caused by misfolding of serum amyloid A protein, which is involved in inflammatory responses.

    • It commonly deposits in the kidney and liver and can affect individuals at any age.

    • It may be involved in long-term inflammatory conditions.

  • Amyloidosis can be challenging to diagnose because it can affect different organs, causing a wide range of symptoms.

What is Cardiac Amyloidosis?

  • Cardiac amyloidosis is a systemic form where protein-based infiltrates deposit in myocardial tissue.

  • The accumulation of amyloid fibrils causes the myocardium to thicken and stiffen, leading to diastolic dysfunction, restrictive cardiomyopathy, and heart failure.

  • Cardiac amyloidosis has been identified as a primary cause of heart failure, particularly unexplained heart failure with preserved ejection fraction (HFpEF) in the elderly.

  • Cardiac amyloidosis is often underdiagnosed, with a delay of 2 or more years from initial presentation to diagnosis.

  • AL and ATTR account for approximately 95% of cardiac amyloid diagnoses.

  • Other forms of systemic amyloidosis rarely affect the heart.

  • Differentiation between AL and ATTR is essential because the therapy and prognosis differ vastly.

  • Untreated, both types can lead to heart failure and reduced life expectancy.

Cardiac AL

  • AL results from plasma cell dyscrasia, the unregulated proliferation of a single plasma cell clone.

  • AL prognosis depends on the number and severity of organs involved, with cardiac involvement having the worst prognosis because of its rapid clinical progression and late diagnosis.

  • Untreated cardiac AL has a median survival of 6 months from the onset of heart failure.

  • Treatment focuses on symptom management and suppressing additional light-chain production, usually involving chemotherapy and immunotherapy.

  • Cardiac AL is relatively rare and typically diagnosed in patients between 40 and 80 years old.

  • Cardiac AL can be associated with other immunoglobulin-related diseases, such as multiple myeloma.

Cardiac ATTR

  • Compared with cardiac AL, there is less evidence of direct toxic effects associated with cardiac ATTR.

  • It is subdivided into wild-type ATTR and variant (hereditary) ATTR.

  • Wild-type ATTR is the most common type of cardiac amyloidosis and occurs with aging.

    • Wild-type ATTR accounts for about 80% of cardiac amyloidosis cases. On autopsy, nearly 30% of patients over 75 years old with HFpEF without an antemortem suspicion of amyloid disease were found to have wild-type ATTR.

    • Wild-type ATTR has been found in 13% of hospitalized patients with HFpEF and left ventricular wall thickness greater than 1.2 cm.

    • Wild-type ATTR occurs predominantly in people over 70 years old and affects men more often than women.

    • Wild-type ATTR is clinically associated with bilateral carpal tunnel syndrome, aortic stenosis, atrial fibrillation, and other conditions resulting in increased wall thickness.

    • The median survival from diagnosis is 57 months.

  • Variant ATTR is inherited from a genetic mutation in the transthyretin gene that affects the amino acid sequence.

    • Over 120 variant ATTR genotypic mutations have been identified.

    • Worldwide, the most common mutation is V30M, which is associated more with sensory or autonomic neuropathy than with cardiomyopathy.

    • In the United States, the V122I mutation, which is more likely to cause cardiomyopathy, is more common. It is estimated that 2 million people in the United States are carriers and that 3%–4% of African Americans carry the gene.

    • Like wild-type cardiac ATTR, variant cardiac ATTR is more common in men and is usually diagnosed between the ages of 55 and 75 years old.

    • It is also associated with bilateral carpal tunnel syndrome along with polyneuropathy.

    • The median survival from diagnosis is 31 months for the V122I form and 69 months for other forms of variant ATTR.

Signs and Symptoms of Cardiac Amyloidosis

  • Untreated, all forms of cardiac amyloidosis result in heart failure due to the restrictive nature of the disease and diastolic dysfunction.

  • Many patients experience the classic symptoms of heart failure:

    • Shortness of breath during exertion and when lying down

    • Swelling in the feet, ankles, and legs

    • Orthostatic hypotension

    • Irregular heart rhythms

    • Lightheadedness

    • Abdominal distension

    • Overall weakness and fatigue

  • If amyloid is deposited in the heart valves, it can lead to regurgitation or stenosis.

  • It is not uncommon to discover that patients being treated for severe aortic stenosis also have ATTR.

  • Treatment for both types of cardiac ATTR includes the management of heart failure symptoms and arrhythmias.

  • New pharmacotherapeutic drugs are available that can help silence, stabilize, or break down errant proteins.

  • Patients may experience red flags, such as numbness, tingling, or pain in the hands or feet.

  • Patients with cardiac amyloidosis may have skin changes, such as thickness or easy bruising.

  • Some patients with AL may demonstrate purple patches around the eyes (periorbital purpura), sometimes called panda or raccoon eyes.

  • Macroglossia, an enlarged tongue that looks rippled along the edge, is a symptom in patients with AL.

  • Patients may experience increased or decreased urination, diarrhea, or constipation because AL can affect the kidneys and gastrointestinal tract.

\text{99mTc}-Pyrophosphate Scan Acquisition

  • Because cardiac amyloidosis eventually results in cardiac dysfunction, a debilitating disease, and because the treatment options vastly differ between ATTR and AL, it is critical to diagnose and differentiate between them.

  • \text{99mTc}-pyrophosphate imaging can efficiently and effectively distinguish between ATTR and cardiac AL.

  • Although the exact mechanism underlying \text{99mTc}-pyrophosphate uptake in cardiac amyloidosis is unknown, ATTR amyloid plaque is thought to contain a higher concentration of microcalcifications that bind with the pyrophosphate, allowing for improved uptake on nuclear cardiac imaging.

  • \text{99mTc}-pyrophosphate imaging has a 97% sensitivity and nearly 100% specificity for identifying cardiac ATTR when the AL form of the disease is ruled out by the serum free light-chain ratio and serum and urine protein electrophoresis with immunofixation tests.

  • Several radiopharmaceuticals and imaging protocols have been used for cardiac amyloidosis imaging over the past 40 years.

  • The American Society of Nuclear Cardiology and other professional medical societies published consensus recommendations to standardize performance and interpretation to improve quality and patient outcomes.

  • The primary indication for \text{99mTc}-pyrophosphate imaging is the evaluation of patients with heart failure and increased left ventricular wall thickness not associated with other conditions or reasons.

  • \text{99mTc}-pyrophosphate imaging is also indicated for men over 60 years old who may be African Americans or patients with HFpEF.

  • Patients with signs of heart failure and a history of bilateral carpal tunnel syndrome, unexplained neuropathy, or atrial arrhythmias are also candidates for \text{99mTc}-pyrophosphate imaging.

  • In addition, \text{99mTc}-pyrophosphate imaging is indicated to differentiate variant from wild-type cardiac ATTR in patients with a suspected or known family history of amyloidosis.

  • Finally, patients who are believed to have cardiac ATTR but have contraindications to cardiac MRI are candidates for \text{99mTc}-pyrophosphate imaging.

  • There are no known contraindications specific to \text{99mTc}-pyrophosphate imaging other than the usual nuclear medicine procedure cautions related to pregnancy, breastfeeding, and other recent nuclear medicine scans.

  • There are no specific patient restrictions before \text{99mTc}-pyrophosphate imaging. Patients may eat, drink, and take their medications as usual.

  • However, patients should be warned about the 3-hour delay between injection and imaging.

  • A thorough patient medical history is crucial for accurate interpretation of \text{99mTc}-pyrophosphate cardiac amyloidosis scans.

Radiopharmaceutical

  • A variety of \text{99mTc}-diphosphonate and pyrophosphate bone-seeking agents, specifically \text{99mTc}-pyrophosphate, \text{99mTc}-3,3-diphosphono-1,2-propanodicarboxylic acid (\text{99mTc}-DPD), and \text{99mTc}-hydroxymethylene diphosphonate (\text{99mTc}-HMDP), can be used to diagnose ATTR cardiomyopathy.

  • In the absence of cardiac amyloidosis or subacute myocardial infarction, these bone tracers do not accumulate in the myocardium.

  • Thus, radionuclide imaging can differentiate cardiac amyloidosis from other conditions that mimic it, such as hypertrophic cardiomyopathy.

  • Although no studies to date have directly compared the 3 tracers, the published literature suggests they can be used interchangeably.

  • \text{99mTc}-DPD and \text{99mTc}-HMDP are predominantly used in Europe because \text{99mTc}-pyrophosphate is not available there.

  • \text{99mTc}-pyrophosphate is used in the United States because the Food and Drug Administration has not approved \text{99mTc}-DPD, and there is limited access to \text{99mTc}-HMDP.

  • \text{99mTc}-methylene diphosphonate has a significantly lower sensitivity and should not be used for cardiac amyloid imaging.

  • The recommended dose is 370–740 MBq (10–20 mCi) administered intravenously.

  • The total radiation exposure from a 555-MBq (15-mCi) dose is approximately 3 mSv.

  • \text{99mTc}-pyrophosphate clears from the blood pool, with rapid uptake in the bone and myocardium.

  • Accumulation of \text{99mTc}-pyrophosphate in the bone continues to increase over time.

  • However, myocardial uptake in amyloid disease peaks at about 1 hour and then slowly begins to decline.

  • The \text{99mTc}-pyrophosphate blood pool clearance rate depends on bone metabolism and renal function.

  • The higher the bone metabolism along with normal renal function, the faster the \text{99mTc}-pyrophosphate clears from the blood pool, improving the semiquantitative and quantitative interpretation of the study.

Acquisition

  • After intravenous injection of the \text{99mTc}-pyrophosphate, both planar and SPECT images of the patient’s chest are obtained 3 hours later.

  • Imaging is usually performed on a standard dual-head g-camera using a 90° detector configuration.

  • Patients are imaged supine with their arms above their head.

  • For cameras with a large field of view, the patient’s shoulders should be near the top of the field of view to visualize the entire ribcage.

  • The planar images include the anterior and left lateral projections.

  • The SPECT acquisition should include as much of the chest as will fit within the field of view.

  • SPECT imaging may be performed using a 180° or 360° acquisition.

  • If SPECT/CT is available, CT attenuation correction is recommended.

  • Whole-body imaging is optional and has been shown to be of benefit, especially when imaging with \text{99mTc}-DPD or \text{99mTc}-HMDP.

  • Whole-body imaging can demonstrate \text{99mTc}-DPD or \text{99mTc}-HMDP uptake in the shoulder and hip girdles, a specific indicator of systemic ATTR.

Summary

  • The recent discovery of the sizable prevalence of cardiac amyloidosis in the population has led to a dramatic increase in the number of laboratories performing cardiac amyloidosis imaging.

  • The lack of published guidelines delineating standardized imaging parameters and interpretation criteria for cardiac amyloidosis imaging led to considerable study variability and the potential for misdiagnoses.

  • The American Society of Nuclear Cardiology, the Society of Nuclear Medicine and Molecular Imaging, and several other professional societies published consensus recommendations for performing and interpreting \text{99mTc} -pyrophosphate cardiac amyloidosis imaging.

  • This article, part 1 of a 3-part series, explains the etiology and characteristics of cardiac amyloid disease so that technologists understand how the intricacies of the disease affect test performance.

  • This article further provides a technical foundation for study acquisition.

  • Part 2 details how to process and quantify the images and justifies some of the technical considerations of \text{99mTc}-pyrophosphate cardiac amyloidosis imaging.

  • Part 3 will put acquisition and data quantification together to describe study interpretation and the diagnosis and treatment of cardiac amyloidosis.