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Introduction to Pharmacology

  • Pharmacology is the study of substances that interact with living systems through chemical processes.

  • Medical pharmacology is the science of substances used to prevent, diagnose, and treat disease.

  • Toxicology is the branch of pharmacology that deals with the undesirable effects of chemicals on living systems.

History of Pharmacology

  • Prehistoric people recognized the beneficial or toxic effects of many plant and animal materials.

  • Early written records list remedies, some of which are still recognized as useful drugs today.

  • Materia Medica, the science of drug preparation and medical uses of drugs, developed as the precursor to pharmacology.

  • François Magendie and Claude Bernard developed the methods of experimental physiology and pharmacology.

  • Advances in chemistry and physiology laid the foundation for understanding how drugs work at the organ and tissue levels.

Pharmacogenomics

  • Pharmacogenomics is the relation of an individual's genetic makeup to their response to specific drugs.

  • Small interfering RNAs (siRNAs) and micro-RNAs (miRNAs) are investigated as therapeutic agents.

  • Antisense oligonucleotides (ANOs) can interfere with the readout of genes and the transcription of RNA.

General Principles of Pharmacology

  • All substances can be toxic under certain circumstances, depending on the usage of the drug.

  • Chemicals in botanicals are no different from chemicals in manufactured drugs, except for the greater proportion of impurities in botanicals.

  • Dietary supplements and therapies promoted as health-enhancing should meet the same standards of efficacy and safety as conventional drugs and medical therapies.

General Principles of Pharmacology

  • A drug is any substance that brings about a change in biologic function through its chemical actions.

  • Receptors are target molecules that drugs interact with.

  • Agonists activate receptors, while antagonists inhibit receptors.

  • Xenobiotics are chemicals that are not synthesized in the body.

  • Poisons are drugs that have almost exclusively harmful effects.

  • Toxins are poisons of biologic origin, synthesized by plants or animals.

Nature of Drugs

  • Drugs vary in size and molecular weight.

  • Drugs must be convertible to polar compounds for easy excretion.

  • Drugs with a molecular weight <100 are rarely selective in their action.

  • Drugs with a molecular weight >1000 are poorly absorbed and poorly distributed.

Drug-Receptor Bonds

  • Drug-receptor bonds can be covalent, electrostatic (ionic, hydrogen, van der Waals), or hydrophobic.

  • The strength of bonds determines the reversibility of the drug's effect.

  • Pralidoxime cannot reverse insecticide poisoning if the bonds formed by the poison have aged and become covalent.

  • Atropine is given in insecticide poisoning to alleviate symptoms.

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Pharmacodynamic Principles

  • Receptors are specific molecules in a biologic system with which drugs interact to produce changes in the function of the system.

  • Receptors must be selective in their ligand-binding characteristics.

  • Receptors must be modified when they bind an agonist to bring about functional change.

  • Receptors are mostly proteins.

Graded Dose-Response Relationship

  • The graded dose-response relationship graph shows the response of a particular receptor-effector system measured against increasing drug concentrations.

  • The graph yields a sigmoid curve when plotted on a semilogarithmic axis.

  • Efficacy (Emax) and potency are derived from this curve.

  • Binding affinity is the fraction of receptors bound by a drug plotted against the log of the drug concentration.

  • The smaller the Kd (concentration required to bind 50% of receptors), the greater the affinity of a drug for its receptor.

  • Emax is the maximal effect achievable with increasing concentration of a drug.

  • EC50 is the concentration of the drug where half of the maximal effect is achieved.

  • Bmax is the maximum percentage of receptors with increasing concentration of the drug.

  • Kd is the concentration where 50% of receptors are occupied.

Quantal Dose-Response Relationship

  • The quantal dose-response relationship determines the minimum dose required to produce a specified response in each member of a population.

  • The quantal dose-response curve shows the fraction of the population that responds at each dose against the log of the dose administered.

  • Median effective (ED50), median toxic (TD50), and median lethal (LD50) doses are derived from this curve.

  • No attempt is made to determine the maximal effect.

Therapeutic Index

  • The therapeutic index is a measure of the safety of a drug.

  • It is the ratio of the median toxic dose (TD50) to the median effective dose (ED50).

  • A higher therapeutic index indicates a safer drug.

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Potency

  • Denotes the amount of drug needed to produce a given effect.

  • Determined mainly by the affinity of the receptor to the drug.

  • Measurement:

    • In graded dose-response curve, it is the dose required to produce 50% of the maximal effect.

    • In quantal dose-response curve, three potency variables are measurable:

      • ED50

      • TD50

      • LD50

Spare Receptors

  • Receptors that do not bind to the drug when the drug concentration is sufficient to produce maximal effect.

  • Present when Kd50 (50% receptors are occupied) is greater than EC50 (50% max effect achieved).

  • Increase sensitivity to agonist because the likelihood of drug receptor interaction increases directly proportional to the number of receptors available.

Factors Affecting Dose-Response Curves

  • Full Agonists:

    • Capable of fully activating the effector system when it binds to the receptor.

    • High affinity for the activated receptor conformation.

    • Sufficiently high concentrations result in all the receptors achieving the activated state.

  • Partial Agonist:

    • Produces less than the full effect, even when it has saturated the receptors.

    • In the presence of an agonist, a partial agonist acts as an inhibitor/antagonist.

  • Inverse Agonist:

    • Drug has a much stronger affinity for the Ri conformation than the Ra state and stabilizes a large fraction in the Ri-D complex.

    • Activation of these agonists leads to mass inhibition.

    • The drug will reduce any constitutive activity, resulting in effects opposite of the effects produced by the full agonist.

  • Antagonist:

    • Do not provoke a biological response by themselves upon binding to a receptor.

    • Blocks or dampens drug response in the presence of an agonist.

  • Classification of Antagonists:

    1. Competitive or Reversible Antagonist:

      • Binds to receptors in a reversible way without activating the effector system.

      • Shifts the dose response curve (DRC) to the right (increased ED50) but same maximal effect is reached.

      • Effects overcome by adding more agonist (surmountable).

    2. Non-competitive or Irreversible Antagonist:

      • Causes downward shift of the DRC.

      • No horizontal shift of DRC (ED50 unchanged) unless spare receptors are present.

      • Not overcome by adding more agonist (insurmountable).

    3. Physiologic Antagonist:

      • Binds to a different receptor, producing an effect opposite to that produced by the drug it is antagonizing.

    4. Chemical Antagonist:

      • Receptors are not involved.

      • Interact directly with the drug being antagonized to remove it or to prevent it from reaching its target.

    5. Allosteric Antagonist:

      • Binds to a different binding site that forms a conformational change in the receptor preventing the agonist from binding.

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Signaling Mechanisms and Drug Actions

  1. Intracellular Receptor:

    • Crosses the plasma membrane and acts on the intracellular receptor.

    • Enzyme

    • Regulator of gene transcription

  2. Transmembrane Receptor:

    • The signal binds to the extracellular domain of a transmembrane protein, thereby activating the enzymatic activity of its cytoplasmic domain.

  3. Enzyme-Linked Receptor:

    • Have extracellular binding sites where ligand or typically hormone or growth factor can attach and thus activate enzymatic activity inside the cell.

    • Most enzyme-linked receptors are of tyrosine kinase.

  4. Ligand-Gated Ion Channel:

    • Signal binds to and directly regulates the opening of an ion channel.

  5. G-Protein Coupled Receptors:

    • Alpha 1 and 2 receptor.

    • The signal binds to a cell-surface receptor linked to an effector enzyme by a G protein.

    • Also called as 7-transmembrane.

    • Ligand binds to receptor.

    • GDP becomes GTP.

    • Alpha is removed from the G-protein coupling.

Requirements for Adenylyl Cyclase

  • Alpha should meet GTP

Three Types of G Protein

  • Gs:

    • Stimulative G protein that activates the enzyme called ADENYLYL CYCLASE.

    • Adenylyl cyclase then produces cyclic AMP which is a very important secondary messenger.

  • Gi:

    • Inhibitory G protein that inhibits ADENYLYL CYCLASE, thus lowers the level of cAMP in the cell.

  • Gq:

    • Contraction due to calcium.

    • Activates a class of enzyme called phospholipases C (PLC).

    • PLC produces two secondary messengers called diacylglycerol (DAG) and inositol triphosphate (IP3).

    • DAG: leads to different responses through activation of protein kinases.

    • IP3: produces various responses by mediating intracellular release of calcium.

  • G-protein coupled receptors, as well as enzyme-linked receptors, have the ability to amplify signals that they receive.

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Variations in Drug Response

  • Tolerance:

    • Continuous activation may lead to depletion of essential substrates.

    • Reversed by repletion of missing substrates.

    • Example: depletion of thiol cofactors in nitroglycerin tolerance, reversible with administration of glutathione.

  • Down Regulation:

    • Long-term reduction in receptor number due to continuous exposure to agonist.

  • Upregulation:

    • Occurs when receptor activation is blocked for prolonged periods.

  • Tachyphylaxis:

    • Responsiveness diminishes rapidly after administration of a drug.

    • Slight delay after first intake.

    • Frequent or continuous exposure to agonists often results in short-term diminution of the receptor response.

    • Examples of drugs that display tachyphylaxis: Metoclopramide, Nitroglycerin, Ephedrine, Nicotine, Dobutamine, Hydralazine, LSD, Desmopressin, Calcitonin.

  • Idiosyncratic Drug Response:

    • One that is infrequently observed in most patients.

    • Example: aplastic anemia with chloramphenicol, cataracts